RNA trans-splicing-mediated COL7A1 repair in a dystrophic epidermolysis bullosa mouse model
Peking, P; Koller, U; Kocher, T; Nystroem, A; Reichelt, J; Bauer, JW; Murauer, EM J INVEST DERMATOL. 2017; 137(10): S229-S229.
Antisense RNA-mediated improvement of SMaRT therapy for KRT14 correction
Liemberger, B; Arzt, C; Hainzl, S; Kocher, T; Hofbauer, JP; Murauer, EM; Bauer, JW; Reichelt, J; Koller, U J INVEST DERMATOL. 2017; 137(10): S229-S229.
Viral antigen-specific pre-vaccination prevents engraftment of tumor cells expressing the cognate antigen in mice
Leb-Reichl, V; Kienzl, M; Stoecklinger, A; Kitzmueller, S; Gratz, IK; Brachtl, G; Zaborsky, N; Reichelt, J; Gruber, C; Hofbauer, JP J INVEST DERMATOL. 2017; 137(10): S286-S286.
CRISPR/Cas9 mediated gene correction of COL7A1
Hainzl, S; Peking, P; Kocher, T; Murauer, EM; Larcher, F; del Rio, M; Duarte, BG; Steiner, M; Klausegger, A; Bauer, JW; Reichelt, J; Koller, U J INVEST DERMATOL. 2017; 137(10): S224-S224.
Extracellular vesicles as biomarkers for the detection of epidermolysis bullosa-associated squamous cell carcinoma
Sun, Y; Woess, K; Wimmer, M; Zauner, R; Feinle, A; Wally, V; South, A; Furihata, T; Hofbauer, JP; Gruber, C J INVEST DERMATOL. 2017; 137(10): S288-S288.
Austrian interdisciplinary Recommendations on the Use of Medications during the Wish to have Children as well as in Pregnancy and Lactation Period – Results of a gastroenterological-rheumatologic-dermatological Consensus
Sautner, J; Puchner, R; Grochenig, HP; Helmy-Bader, Y; Hermann, J; Hogenauer, C; Koch, R; Reinisch, S; Studnicka-Benke, A; Weger, W; Dejaco, C WIEN KLIN WOCHENSCHR. 2017; 129: S132-S132.
EVALUATION OF SALVAGE INDUCTION CHEMOTHERAPY REGIMENS IN MYELODYSPLASTIC SYNDROME AND ACUTE MYELOID LEUKEMIA AFTER HYPOMETHYLATING AGENT TREATMENT FAILURE
Ball, B; Komrokji, R; Ades, L; Sekeres, M; DeZern, A; Pleyer, L; Vey, N; Almeida, A; Germing, U; Cluzeau, T; Platzbecker, U; Gore, S; Fenaux, P; Prebet, T LEUKEMIA RES. 2017; 55: S58-S59.
Ex vivo COL7A1 editing via CRISPR/Cas9 in recessive dystrophic epidermolysis bullosa
Hainzl, S; Peking, P; Kocher, T; Murauer, E; Larcher, F; Duarte, B; Steiner, M; Bauer, J; Reichelt, J; Koller, U J INVEST DERMATOL. 2017; 137(5): S92-S92.
Enhanced genome editing using split Staphylococcus aureus Cas9 delivered in self-complementary AAV vectors
Liemberger, B; Arzt, C; Hainzl, S; Wally, V; Kocher, T; Hofbauer, JP; Murauer, EM; Bauer, JW; Reichelt, J; Koller, U HUM GENE THER. 2017; 28(12): A63-A63.
Highly efficient and safe CRISPR/Cas9n double nicking-mediated KRT14 repair in epidermolysis bullosa simplex keratinocytes
Kocher, T; Peking, P; Klausegger, A; Murauer, EM; Hofbauer, JP; Wally, V; Lettner, T; Hainzl, S; Ablinger, M; Bauer, JW; Reichelt, J; Koller, U HUM GENE THER. 2017; 28(12): A57-A57.